Tag: Rare Diseases
FDA Approval: Ionis Rare Disease Therapy Lowers Triglycerides
Ionis Pharmaceuticals has achieved a significant milestone by obtaining FDA approval for their groundbreaking therapy, Tryngolza, designed to combat a rare and fatal genetic...
Readers’ Opinions on Covid, Trump, Rare Diseases, and Institutional Neutrality: A Comprehensive Overview
First Opinion is STAT’s platform for interesting, illuminating, and provocative articles about the life sciences writ large, written by biotech insiders, health care workers,...
Understanding Angelman Syndrome: What You Need to Know & Colin Farrell’s Son’s Battle
Colin Farrell, the well-known actor, is taking a step forward in raising awareness for a rare genetic condition known as Angelman syndrome. This move...
Studying Rare Congenital Heart Defects: $13M Project Commits to Investigate Biological Mechanisms
Single ventricle heart disease is a rare condition that affects about 1 in 15,000 babies born in the U.S. This congenital defect occurs when...
BREAKING NEWS
Medicare Coverage of Wegovy Should Include, But Not Negotiate Price
Title: Biden Administration's Decision on Wegovy Medicare Coverage Sparks ControversyPresident Biden's recent announcement regarding the Medicare coverage of Wegovy, a GLP-1 obesity medication, has...
