Tag: Medical Research
Ending 23andMe’s Drug Discovery Dream: What Went Wrong?
23andMe, the genetics company that many people have been excited about, recently made a big announcement. The company has decided to stop working on creating new medicines and will be letting go of 40%...
Assessing the Cost-Effectiveness of Alzheimer’s Drug Donanemab in the U.K.
The recent decision by the U.K.'s National Institute for Health and Care Excellence (NICE) regarding the cost-effectiveness of the Alzheimer's drug Donanemab, also known as Kisunla, has raised concerns about its accessibility to patients....
Overcoming Challenges of Traditional Trials in Ultra-Rare Diseases: The Case of Barth Syndrome
Ultragenyx's founder and CEO, Kakkis, is at the forefront of developing another treatment for an ultra-rare disease called Barth syndrome. This genetic disorder affects around 200 boys worldwide and is caused by a mutation...
Accurate Alzheimer’s Diagnosis: Blood Test with 90% Success Rate
Scientists have recently made a significant advancement in the quest for a simple blood test to accurately diagnose Alzheimer's disease. The study, published in the journal JAMA, revealed that the blood test was approximately...